named programs · 4 · from sources
What they call their work
Community Support Network
Provides emotional support and connection for individuals diagnosed with NLSD-M to reduce isolation and share experiences
Research Advocacy and Collaboration
Facilitates partnerships between physicians, researchers, and pharmaceutical companies to advance NLSD-M research and treatment development
Scientific Advisory Board
Comprised of medical experts who provide clinical and scientific guidance to support the foundation’s mission and research initiatives
Strength and Conditioning Guidance
Offers evidence-based recommendations for strength training and aerobic conditioning tailored to individuals with NLSD-M to maintain functional mobility
activities · 4 groups
What they do
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Rare Genetic Disease Research and Advocacy 4 activities
- Advancing treatment development for NLSD-MWorks to advance the development of treatments for Neutral Lipid Storage Disease with Myopathy (NLSD-M), including launching a nonprofit organization dedicated to finding and developing therapies and supporting research efforts toward a cure.
- Building capacity for rare disease researchSupports rare disease research by fostering patient communities to drive collaborative efforts toward cures.
- Conducting gene therapy research for NLSD-MConducting research to develop a human gene therapy for Neutral Lipid Storage Disease with Myopathy (NLSD-M), including proof of concept, safety, and efficacy testing in patient cells and mouse models, with pioneering work on dual gene AAV therapies to restore gene function and rebuild muscle mass.
- Raising awareness of NLSD-MRaises public and global awareness about Neutral Lipid Storage Disease with Myopathy (NLSD-M), a rare disease currently without a cure, to promote understanding and engagement.
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Charity Golf Tournament Fundraiser 1 activity
- Fundraising for NLSD-M research and supportHosts an annual golf outing and facilitates global fundraising opportunities to support NLSD-M research and programs; encourages use of employer matching gift programs to increase donation impact.
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Peer-Led Mental Health Support Groups 1 activity
- Providing emotional and community support for NLSD-M patientsProvides emotional support and fosters community connections for individuals diagnosed with NLSD-M to reduce isolation, help them adjust to life after diagnosis, and offer a space to share experiences.
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Uncategorized 1 activity
- Delivering physical and nutritional health support for NLSD-MProvides strength training and conditioning programs to prevent muscle atrophy and deconditioning, along with supplement recommendations and Functional Nutrition Assessments to improve mobility, energy, strength, and dietary planning for individuals with NLSD-M.
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financials · form 990 · fy2025
revenue
Total revenue$165K
Contributions & grants$91K55%
Program service revenue$00%
Investment income$00%
Other revenue$74K
expenses
Total expenses$26K
Program expenses18%
Admin / overhead56%
Fundraising26%
Salaries & benefits$0
Grants paid out$0
Largest expense lineProfessional Fees
balance sheet
Total assets$238K
Cash$234K
Investments$0
Liabilities$0
Net assets$238K
Liquid reserves109.5 mo
2 years on record · 2024–2025 · YoY revenue +56.3%
leadership · form 990 part vii · fy2025
Who runs it
board members · 4
- DOMENIC CERVINI — VICE PRESIDENT
- GABRIELLE ZEPPIERI — PRESIDENT
- GINO ZEPPIERI — TREASURER
- MARIA ZEPPIERI — VICE PRESIDENT/SECRETARY
relationships · 19
Who they work with
- A Nice Sign Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Alfie's Rocky Point Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Boutique Suarez Co Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Boutique Suarez Co. Partner — Partner for selling custom-made foundation merchandise, including a foundation bracelet
- CJ Hand Therapy Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Cel-Pep Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Del Fiore Italian Market Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Fetch Doggies Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Four Seasons Sunrooms of Long Island Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- G. Craig Construction Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Moriches Field Brewing Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Nationwide Children’s Hospital Partner — Hosts the Center for Gene Therapy where the Martin Lab conducts research on NLSD-M gene therapy.
- Osaka University Partner — Collaborates with researchers from Osaka University's Graduate School of Medicine and Osaka University Hospital on NLSD-M.
- Padova University Graduate School of Medicine Partner — Collaborates with the Department of Neurosciences at Padova University Graduate School of Medicine, Italy.
- Reisenauer Precision Medicine Fund Funder — Provided funding for the first year of the NLSD-M gene therapy research project.
- San Filipo Neri Hospital Partner — Collaborates with the Neuromuscular and Rare Neurological Disease Center at San Filipo Neri Hospital in Rome, Italy.
- Stony Brook University Hospital Government — Dr. Simona Treidler is a Clinical Assistant Professor in Neurology & Pediatrics at SBUH, indicating an institutional affiliation
- Tattoos by Nick Fierro Partner — Partner organization that donates services and/or time to support GWW NLSDM CORP DBA Gabby's Wonderful World.
- Wu Wei Wellness Partner — Collaborates to provide supplement guidance, nutritional assessments, and holistic care for individuals with NLSD-M.
strategies · 4
How they approach the work
Named approaches extracted from this org’s sources. Where others share an approach, follow it to see the full set of orgs running it.
- Community Support as Therapeutic Interventionmethodology: community_support_for_rare_diseaseBy fostering emotional support and community connection among individuals with NLSD-M, the organization reduces isolation and improves well-being, leveraging shared experiences to strengthen resilience and engagement in care.
- Curative Gene Therapy Translationmethodology: curative-gene-therapy-translationBy developing gene therapies specifically for NLSD-M and advancing them toward clinical use, the organization aims to achieve curative outcomes, addressing the root cause of the disease rather than just symptoms.
- Holistic and Integrative Clinical Approachmethodology: holistic-integrative-medicineBy integrating functional nutrition and holistic medicine—including macronutrient balancing and Traditional Chinese Medicine—the organization supports metabolic and systemic health, aiming to slow progression and improve quality of life in NLSD-M patients.
- Patient-Led Research Advocacy and Fundingmethodology: patient_led_funding_advocacyBy positioning patients and families at the forefront of funding advocacy, the organization drives investment in NLSD-M research and therapy development, accelerating progress where traditional markets fail due to rarity.